A cure for one.

The article discusses gene therapy for rare diseases. Particular focus is given to how those with rare diseases, including Canavan, which is caused by an error in a single gene, are often forced to pay for these treatments on their own. Additional topics discussed include Jennie and Gary Landsman, whose children have been inflicted with Canavan, how Canavan is common amongst those of Ashkenazi Jewish descent, and the work of researcher named Steven Gray.