- Tytuł:
- Gene-replacement therapy (GRT) in spinal muscular atrophy type 1 (SMA1): Long-term follow-up from the onasemnogene abeparvovec phase 1/2A clinical trial
- Autorzy:
- Źródło:
- In Journal of the Neurological Sciences 15 October 2019 405 Supplement:271-271
Czasopismo naukowe