- Tytuł:
- Baseline Characteristics of Fabry Disease "Amenable" Migalastat Patients in Argentinian Cohort.
- Autorzy:
- Źródło:
- Global health, epidemiology and genomics [Glob Health Epidemiol Genom] 2024 Feb 19; Vol. 2024, pp. 9293896. Date of Electronic Publication: 2024 Feb 19 (Print Publication: 2024).
- Typ publikacji:
- Journal Article
- MeSH Terms:
-
Fabry Disease*/epidemiology
Fabry Disease*/genetics
Fabry Disease*/drug therapy
1-Deoxynojirimycin/*analogs & derivatives
Adult ; Humans ; Male ; Female ; 1-Deoxynojirimycin/therapeutic use ; alpha-Galactosidase/genetics ; alpha-Galactosidase/metabolism ; alpha-Galactosidase/therapeutic use ; Pain/chemically induced ; Pain/drug therapy
Czasopismo naukowe