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Wyświetlanie 1-8 z 8
Tytuł:
Part 5: Allogeneic HSCT in refractory SJIA with lung disease; recent cases from centers in North America & Europe.
Autorzy:
Grom AA; Division of Rheumatology, Cincinnati Children's Hospital Medical Center, University of Cincinnati, Cincinnati, OH, USA. .
Canna SW; Rheumatology & Immune Dysregulation, The Children's Hospital of Philadelphia, Philadelphia, PA, USA.
Abu-Arja RF; Department of BMT, Nationwide Children's Hospital, Columbus, OH, USA.
Sinha R; Systemic JIA Foundation, Cincinnati, OH, USA.
Peixoto L; Systemic JIA Foundation, Cincinnati, OH, USA.
Cannizzaro E; Department of Rheumatology, University Children's Hospital, Zurich, Switzerland.
Chandrakasan S; Department of Pediatrics, School of Medicine, Emory University, Atlanta, GA, USA.; Aflac Cancer and Blood Disorders Center, Children's Healthcare of Atlanta, Emory University, Atlanta, GA, USA.
Driest K; Department of Rheumatology, Nationwide Children's Hospital, Columbus, OH, USA.
Marsh R; Division of Bone Marrow Transplantation and Immune Deficiency, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
Neven B; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants- Malades University Hospital, Paris, France.; Université Paris-Cité, Paris, France.
Onel K; Department of Rheumatology, HSS, New York City, NY, USA.
Prahalad S; Department of Pediatrics, School of Medicine, Emory University, Atlanta, GA, USA.
Prockop S; Dana Farber/Boston Childrens Hospital Center for Cancer and Blood Disorders, Boston, MA, USA.
Quartier P; Pediatric Hematology-Immunology and Rheumatology Department, Necker-Enfants- Malades University Hospital, Paris, France.; Université Paris-Cité, Paris, France.
Roth J; Kantonsspital Luzern, University of Luzern, Luzern, Switzerland.
Schulert G; Division of Rheumatology, Cincinnati Children's Hospital Medical Center, University of Cincinnati, Cincinnati, OH, USA.
Silva JMF; Department of BMT, Great Ormond Street Hospital for Children, London, UK.
Wall D; 16. Blood and Marrow Transplant/Cellular Therapy, Division of Haematology/Oncology, Hospital for Sick Children Toronto, Toronto, Canada.
Zeilhofer U; Department of BMT, University Children's Hospital, Zurich, Switzerland.
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Źródło:
Pediatric rheumatology online journal [Pediatr Rheumatol Online J] 2024 Jan 05; Vol. 21 (Suppl 1), pp. 86. Date of Electronic Publication: 2024 Jan 05.
Typ publikacji:
Journal Article
MeSH Terms:
Lung Diseases*/therapy
Hematopoietic Stem Cell Transplantation*/adverse effects
Humans ; Europe ; North America ; Registries
Czasopismo naukowe
Tytuł:
The 4 NextGen therapies of SJIA and MAS, part 4: it is time for IL-18 based trials in systemic juvenile idiopathic arthritis?
Autorzy:
Canna SW; Rheumatology & Immune Dysregulation, The Children's Hospital of Philadelphia, Philadelphia, PA, USA. .
De Benedetti F; Division of Rheumatology, Ospedale Pediatrico Bambino Gesù, Rome, Italy.
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Źródło:
Pediatric rheumatology online journal [Pediatr Rheumatol Online J] 2024 Jan 05; Vol. 21 (Suppl 1), pp. 79. Date of Electronic Publication: 2024 Jan 05.
Typ publikacji:
Journal Article
MeSH Terms:
Arthritis, Juvenile*/drug therapy
Humans ; Interleukin-18 ; Consensus ; Disease Progression ; Biomarkers
Czasopismo naukowe
Tytuł:
Sepsis with liver dysfunction and coagulopathy predicts an inflammatory pattern of macrophage activation.
Autorzy:
Anderko RR; Department of Critical Care Medicine, University of Pittsburgh, Pittsburgh, PA, USA.
Gómez H; Department of Critical Care Medicine, University of Pittsburgh, Pittsburgh, PA, USA. .; Center for Critical Care Nephrology, Department of Critical Care Medicine, University of Pittsburgh, School of Medicine, 3550 Terrace Street, 6th floor Scaife Hall, Pittsburgh, PA, 15261, USA. .
Canna SW; RK Mellon Institute and Pediatric Rheumatology, Children's Hospital of Pittsburgh of University of Pittsburgh Medical Center, Pittsburgh, PA, USA.; Division of Rheumatology, The Children's Hospital of Philadelphia, Philadelphia, PA, USA.
Shakoory B; Translational Autoinflammatory Disease Studies Unit, Laboratory of Clinical Immunology and Microbiology, National Institute of Allergy and Infectious Diseases, Bethesda, MD, USA.
Angus DC; Department of Critical Care Medicine, University of Pittsburgh, Pittsburgh, PA, USA.
Yealy DM; Department of Emergency Medicine, University of Pittsburgh, Pittsburgh, PA, USA.
Huang DT; Department of Critical Care Medicine, University of Pittsburgh, Pittsburgh, PA, USA.
Kellum JA; Department of Critical Care Medicine, University of Pittsburgh, Pittsburgh, PA, USA.; Center for Critical Care Nephrology, Department of Critical Care Medicine, University of Pittsburgh, School of Medicine, 3550 Terrace Street, 6th floor Scaife Hall, Pittsburgh, PA, 15261, USA.
Carcillo JA; Department of Critical Care Medicine, University of Pittsburgh, Pittsburgh, PA, USA.; Center for Critical Care Nephrology, Department of Critical Care Medicine, University of Pittsburgh, School of Medicine, 3550 Terrace Street, 6th floor Scaife Hall, Pittsburgh, PA, 15261, USA.
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Corporate Authors:
ProCESS Investigators
Źródło:
Intensive care medicine experimental [Intensive Care Med Exp] 2022 Feb 21; Vol. 10 (1), pp. 6. Date of Electronic Publication: 2022 Feb 21.
Typ publikacji:
Journal Article
Czasopismo naukowe
Tytuł:
Proceedings from the 2 Next Gen Therapies for Systemic Juvenile Idiopathic Arthritis and Macrophage Activation Syndrome symposium held on October 3-4, 2019.
Autorzy:
Canna SW; University of Pittsburgh, Pittsburg, PA, USA.
Schulert GS; Division of Rheumatology, Cincinnati Children's Hospital Medical Center and Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, USA. .
de Jesus A; Intramural Research Program, National Institute of Allergy and Infectious Diseases, NIH, North Bethesda, USA.
Pickering A; Harvard Medical School, Boston, MA, USA.
Brunner H; Division of Rheumatology, Cincinnati Children's Hospital Medical Center and Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, USA.
Gadina M; Intramural Research Program, National Institute of Allergy and Infectious Diseases, NIH, North Bethesda, USA.
Levine S; Intramural Research Program, National Institute of Allergy and Infectious Diseases, NIH, North Bethesda, USA.
Goldbach-Mansky R; Intramural Research Program, National Institute of Allergy and Infectious Diseases, NIH, North Bethesda, USA.
Boutelle J; SJIA Foundation, Cincinnati, USA.
Sinha R; SJIA Foundation, Cincinnati, USA.
DeBenedetti F; Ospedale Pediatrico Bambino Gesù, Rome, Italy.
Grom A; Division of Rheumatology, Cincinnati Children's Hospital Medical Center and Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, USA. .
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Corporate Authors:
NextGen 2019 Participants
Źródło:
Pediatric rheumatology online journal [Pediatr Rheumatol Online J] 2020 Jul 15; Vol. 18 (Suppl 1), pp. 53. Date of Electronic Publication: 2020 Jul 15.
Typ publikacji:
Congress
MeSH Terms:
Arthritis, Juvenile/*therapy
Macrophage Activation Syndrome/*therapy
Arthritis, Juvenile/diagnosis ; Arthritis, Juvenile/pathology ; Biomarkers ; Child ; Child, Preschool ; Disease Progression ; Humans ; Infant ; Macrophage Activation Syndrome/diagnosis ; Macrophage Activation Syndrome/pathology
Tytuł:
The NLRC4 Inflammasome.
Autorzy:
Duncan JA; Division of Infectious Diseases, Department of Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC, USA.
Canna SW; Pediatric Rheumatology & RK Mellon Institute for Pediatric Research, Children's Hospital of Pittsburgh of UPMC, Pittsburgh, PA, USA.
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Źródło:
Immunological reviews [Immunol Rev] 2018 Jan; Vol. 281 (1), pp. 115-123.
Typ publikacji:
Journal Article; Review
MeSH Terms:
Autoimmune Diseases/*metabolism
CARD Signaling Adaptor Proteins/*metabolism
Calcium-Binding Proteins/*metabolism
Familial Mediterranean Fever/*genetics
Infections/*metabolism
Inflammasomes/*metabolism
Inflammation/*metabolism
Pyrin/*metabolism
Animals ; Autoimmune Diseases/genetics ; Humans ; Pyrin/genetics ; Signal Transduction
Czasopismo naukowe
Tytuł:
New monogenic autoinflammatory diseases--a clinical overview.
Autorzy:
Canna SW; Autoinflammatory Pathogenesis Unit, National Institute of Arthritis and Musculoskeletal and Skin Diseases, NIH, Bldg. 10, room 13c103, 10 Center Dr., Bethesda, MD, 20892, USA, scott.canna@nih.gov.
Goldbach-Mansky R
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Źródło:
Seminars in immunopathology [Semin Immunopathol] 2015 Jul; Vol. 37 (4), pp. 387-94. Date of Electronic Publication: 2015 May 12.
Typ publikacji:
Journal Article; Research Support, N.I.H., Intramural; Review
MeSH Terms:
Hereditary Autoinflammatory Diseases/*diagnosis
Hereditary Autoinflammatory Diseases/*etiology
Autoimmune Diseases/diagnosis ; Autoimmune Diseases/genetics ; Autoimmune Diseases/immunology ; Autoimmune Diseases/metabolism ; Hereditary Autoinflammatory Diseases/metabolism ; Humans ; Inflammation/diagnosis ; Inflammation/genetics ; Inflammation/immunology ; Inflammation/metabolism ; Interferons/metabolism ; Interleukin-18/metabolism ; Macrophage Activation Syndrome/diagnosis ; Macrophage Activation Syndrome/genetics ; Macrophage Activation Syndrome/immunology ; Macrophage Activation Syndrome/metabolism ; Mutation ; Phenotype ; Proteasome Endopeptidase Complex/metabolism ; Signal Transduction
Czasopismo naukowe
Tytuł:
An activating NLRC4 inflammasome mutation causes autoinflammation with recurrent macrophage activation syndrome.
Autorzy:
Canna SW; Molecular Immunology and Inflammation Branch, National Institute for Arthritis and Musculoskeletal and Skin Diseases (NIAMS), US National Institutes of Health (NIH), Bethesda, Maryland, USA.
de Jesus AA; Translational Autoinflammatory Disease Section, NIAMS, NIH, Bethesda, Maryland, USA.
Gouni S; Molecular Immunology and Inflammation Branch, National Institute for Arthritis and Musculoskeletal and Skin Diseases (NIAMS), US National Institutes of Health (NIH), Bethesda, Maryland, USA.
Brooks SR; Biodata Mining and Discovery Section, Office of Science and Technology, NIAMS, NIH, Bethesda, Maryland, USA.
Marrero B; Translational Autoinflammatory Disease Section, NIAMS, NIH, Bethesda, Maryland, USA.
Liu Y; Translational Autoinflammatory Disease Section, NIAMS, NIH, Bethesda, Maryland, USA.
DiMattia MA; Laboratory of Structural Biology, NIAMS, NIH, Bethesda, Maryland, USA.
Zaal KJ; Light Imaging Section, Office of Science and Technology, NIAMS, NIH, Bethesda, Maryland, USA.
Sanchez GA; 1] Translational Autoinflammatory Disease Section, NIAMS, NIH, Bethesda, Maryland, USA. [2] Office of the Clinical Director, NIAMS, NIH, Bethesda, Maryland, USA.
Kim H; Translational Autoinflammatory Disease Section, NIAMS, NIH, Bethesda, Maryland, USA.
Chapelle D; 1] Translational Autoinflammatory Disease Section, NIAMS, NIH, Bethesda, Maryland, USA. [2] Office of the Clinical Director, NIAMS, NIH, Bethesda, Maryland, USA.
Plass N; 1] Translational Autoinflammatory Disease Section, NIAMS, NIH, Bethesda, Maryland, USA. [2] Office of the Clinical Director, NIAMS, NIH, Bethesda, Maryland, USA.
Huang Y; Translational Autoinflammatory Disease Section, NIAMS, NIH, Bethesda, Maryland, USA.
Villarino AV; Molecular Immunology and Inflammation Branch, National Institute for Arthritis and Musculoskeletal and Skin Diseases (NIAMS), US National Institutes of Health (NIH), Bethesda, Maryland, USA.
Biancotto A; Center for Human Immunology, National Heart, Lung, and Blood Institute, NIH, Bethesda, Maryland, USA.
Fleisher TA; Department of Laboratory Medicine, NIH Clinical Center, Bethesda, Maryland, USA.
Duncan JA; Infectious Diseases, University of North Carolina School of Medicine, Chapel Hill, North Carolina, USA.
O'Shea JJ; Molecular Immunology and Inflammation Branch, National Institute for Arthritis and Musculoskeletal and Skin Diseases (NIAMS), US National Institutes of Health (NIH), Bethesda, Maryland, USA.
Benseler S; Pediatric Rheumatology, Alberta Children's Hospital and University of Calgary, Calgary, Alberta, Canada.
Grom A; Pediatric Rheumatology, Cincinnati Children's Hospital and University of Cincinnati, Cincinnati, Ohio, USA.
Deng Z; Biodata Mining and Discovery Section, Office of Science and Technology, NIAMS, NIH, Bethesda, Maryland, USA.
Laxer RM; Pediatric Rheumatology, Hospital for Sick Children, Toronto, Ontario, Canada.
Goldbach-Mansky R; Translational Autoinflammatory Disease Section, NIAMS, NIH, Bethesda, Maryland, USA.
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Źródło:
Nature genetics [Nat Genet] 2014 Oct; Vol. 46 (10), pp. 1140-6. Date of Electronic Publication: 2014 Sep 14.
Typ publikacji:
Case Reports; Journal Article; Research Support, N.I.H., Intramural; Research Support, Non-U.S. Gov't
MeSH Terms:
Mutation, Missense*
CARD Signaling Adaptor Proteins/*genetics
Calcium-Binding Proteins/*genetics
Inflammasomes/*genetics
Inflammation/*genetics
Macrophage Activation Syndrome/*genetics
Amino Acid Sequence ; Child ; Exome/genetics ; Female ; Gene Expression Profiling ; Humans ; Inflammation/blood ; Interleukin-18/blood ; Interleukin-18/metabolism ; Macrophage Activation Syndrome/blood ; Macrophages/metabolism ; Molecular Sequence Data ; Oligonucleotide Array Sequence Analysis ; Sequence Analysis, DNA ; Sequence Homology, Amino Acid
Czasopismo naukowe
Tytuł:
A 17 year old with isolated proximal tibiofibular joint arthritis.
Autorzy:
Canna SW; Division of Rheumatology The Children's Hospital of Philadelphia, 3405 Civic Center Blvd, Philadelphia, PA, 19104, USA. .
Chauvin NA
Burnham JM
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Źródło:
Pediatric rheumatology online journal [Pediatr Rheumatol Online J] 2013 Jan 09; Vol. 11 (1), pp. 1. Date of Electronic Publication: 2013 Jan 09.
Typ publikacji:
Journal Article
Czasopismo naukowe
    Wyświetlanie 1-8 z 8

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