- Tytuł:
- Organic Synthesis and Current Understanding of the Mechanisms of CFTR Modulator Drugs Ivacaftor, Tezacaftor, and Elexacaftor.
- Autorzy:
- Źródło:
- Molecules (Basel, Switzerland) [Molecules] 2024 Feb 10; Vol. 29 (4). Date of Electronic Publication: 2024 Feb 10.
- Typ publikacji:
- Journal Article; Review
- MeSH Terms:
-
Cystic Fibrosis Transmembrane Conductance Regulator*/metabolism
Cystic Fibrosis*/drug therapy
Cystic Fibrosis*/genetics
Cystic Fibrosis*/metabolism
Aminopyridines*
Indoles*
Pyrazoles*
Pyridines*
Pyrrolidines*
Quinolones*
Humans ; Quality of Life ; Benzodioxoles/pharmacology ; Benzodioxoles/therapeutic use ; Aminophenols/pharmacology ; Aminophenols/therapeutic use ; Mutation ;Chemistry Techniques ,Synthetic
Czasopismo naukowe