- Tytuł:
-
Pre-clinical evaluation of three non-viral gene transfer agents for
cystic fibrosis after aerosol delivery to the ovine lung. - Autorzy:
- Źródło:
- Gene therapy [Gene Ther] 2011 Oct; Vol. 18 (10), pp. 996-1005. Date of Electronic Publication: 2011 Apr 21.
- Typ publikacji:
- Comparative Study; Evaluation Study; Journal Article; Research Support, Non-U.S. Gov't
- MeSH Terms:
-
Gene Transfer Techniques*
Cystic Fibrosis /*therapyCystic Fibrosis Transmembrane Conductance Regulator/*genetics
Genetic Therapy/*methods
Liposomes/*administration & dosage
Nanoparticles/*administration & dosage
Polyethyleneimine/*administration & dosage
Administration, Inhalation ; Animals ;Cystic Fibrosis /genetics ;Cystic Fibrosis Transmembrane Conductance Regulator/metabolism ; DNA, Complementary/administration & dosage ; DNA, Complementary/genetics ; Humans ; Polyethylene Glycols ; RNA, Messenger/metabolism ; Sheep
Czasopismo naukowe