- Tytuł:
- P68 Outcomes in patients with spinal muscular atrophy (SMA) and four or more SMN2 copies treated with onasemnogene abeparvovec: findings from RESTORE
- Autorzy:
- Źródło:
- In Neuromuscular Disorders October 2023 33 Supplement 1:S133-S133
Czasopismo naukowe