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Wyszukujesz frazę ""Gene Transfer Techniques"" wg kryterium: Temat


Tytuł:
A first step toward gene therapy for hemophilia B?
Autorzy:
Marx J
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Źródło:
Science (New York, N.Y.) [Science] 1993 Oct 01; Vol. 262 (5130), pp. 29-30.
Typ publikacji:
Comment; News
MeSH Terms:
Genetic Therapy*
Factor IX/*genetics
Hemophilia B/*therapy
Animals ; Cloning, Molecular ; Dogs ; Factor IX/biosynthesis ; Gene Transfer Techniques ; Genetic Vectors ; Hemophilia A/genetics ; Hemophilia A/therapy ; Hemophilia B/genetics ; Hepatectomy ; Humans ; Liver/metabolism ; Liver Regeneration ; Retroviridae/genetics
Periodyk
Tytuł:
In vivo gene therapy of hemophilia B: sustained partial correction in factor IX-deficient dogs.
Autorzy:
Kay MA; Department of Molecular Genetics, Baylor College of Medicine, Houston, TX 77030.
Rothenberg S
Landen CN
Bellinger DA
Leland F
Toman C
Finegold M
Thompson AR
Read MS
Brinkhous KM
et. al.
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Źródło:
Science (New York, N.Y.) [Science] 1993 Oct 01; Vol. 262 (5130), pp. 117-9.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
MeSH Terms:
Genetic Therapy*
Factor IX/*genetics
Hemophilia B/*therapy
Liver/*metabolism
Animals ; Cell Line ; Dogs ; Factor IX/analysis ; Factor IX/biosynthesis ; Gene Transfer Techniques ; Genetic Vectors ; Hemophilia B/blood ; Hemophilia B/genetics ; Hepatectomy ; Partial Thromboplastin Time ; Retroviridae/genetics ; Whole Blood Coagulation Time
Czasopismo naukowe
Tytuł:
Germ-line gene modification and disease prevention: some medical and ethical perspectives.
Autorzy:
Wivel NA; Office of Recombinant DNA Activities, National Institutes of Health, Bethesda, MD 20892.
Walters L
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Źródło:
Science (New York, N.Y.) [Science] 1993 Oct 22; Vol. 262 (5133), pp. 533-8.
Typ publikacji:
Journal Article; Review
MeSH Terms:
Blastocyst*
Ethics, Medical*
Gene Transfer Techniques*
Genetic Therapy*
Germ Cells*
Genetic Diseases, Inborn/*prevention & control
Animal Experimentation ; Animals ; Beneficence ; Cultural Diversity ; Eye Neoplasms/prevention & control ; Health ; Humans ; Lesch-Nyhan Syndrome/prevention & control ; Leukodystrophy, Metachromatic/prevention & control ; Patient Selection ; Personal Autonomy ; Retinoblastoma/prevention & control ; Risk Assessment ; Social Responsibility ; Tay-Sachs Disease/prevention & control
Czasopismo naukowe
Tytuł:
The conserved pre-mRNA splicing factor U2AF from Drosophila: requirement for viability.
Autorzy:
Kanaar R; Department of Molecular and Cell Biology, University of California, Berkeley 94720.
Roche SE
Beall EL
Green MR
Rio DC
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Źródło:
Science (New York, N.Y.) [Science] 1993 Oct 22; Vol. 262 (5133), pp. 569-73.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S.; Research Support, U.S. Gov't, P.H.S.
MeSH Terms:
Nuclear Proteins*
RNA Splicing*
Drosophila melanogaster/*genetics
RNA Precursors/*metabolism
Ribonucleoproteins/*genetics
Amino Acid Sequence ; Animals ; Base Sequence ; Conserved Sequence ; DNA, Complementary ; Drosophila melanogaster/growth & development ; Female ; Gene Transfer Techniques ; Genes, Insect ; Genes, Lethal ; In Situ Hybridization ; Male ; Molecular Sequence Data ; Mutation ; RNA/metabolism ; Recombinant Proteins/metabolism ; Ribonucleoproteins/chemistry ; Ribonucleoproteins/metabolism ; Sequence Alignment ; Splicing Factor U2AF
Czasopismo naukowe
Tytuł:
Tethering ribozymes to a retroviral packaging signal for destruction of viral RNA.
Autorzy:
Sullenger BA; Department of Chemistry and Biochemistry, Howard Hughes Medical Institute, University of Colorado, Boulder 80309.
Cech TR
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Źródło:
Science (New York, N.Y.) [Science] 1993 Dec 03; Vol. 262 (5139), pp. 1566-9.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't
MeSH Terms:
RNA, Catalytic/*genetics
RNA, Viral/*metabolism
3T3 Cells ; Animals ; Base Sequence ; Biological Transport ; Cell Line ; Gene Transfer Techniques ; Genetic Vectors/genetics ; Mice ; Molecular Sequence Data ; Moloney murine leukemia virus/genetics ; RNA, Catalytic/administration & dosage ; RNA, Catalytic/metabolism ; RNA, Messenger/metabolism ; beta-Galactosidase/genetics
Czasopismo naukowe
Tytuł:
Cis-acting elements reinforcing the activity of the estrogen-response element in the very-low-density apolipoprotein II gene promoter.
Autorzy:
Schippers IJ; Department of Biochemistry, University of Groningen, The Netherlands.
Kloppenburg M
van Waardenburg R
Ab G
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Źródło:
European journal of biochemistry [Eur J Biochem] 1994 Apr 01; Vol. 221 (1), pp. 43-51.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't
MeSH Terms:
Promoter Regions, Genetic*
Apolipoproteins/*genetics
Estrogens/*pharmacology
Lipoproteins, VLDL/*genetics
Animals ; Base Sequence ; Binding Sites ; Chickens ; DNA/chemistry ; DNA/metabolism ; DNA Mutational Analysis ; Gene Deletion ; Gene Expression Regulation/drug effects ; Gene Transfer Techniques ; Genes, Reporter ; Liver Neoplasms, Experimental ; Molecular Sequence Data ; Plasmids ; Receptors, Estrogen/physiology ; Tumor Cells, Cultured
Czasopismo naukowe
Tytuł:
Cloning, expression and tissue distribution of rat platelet-activating-factor-receptor cDNA.
Autorzy:
Bito H; Department of Biochemistry, Faculty of Medicine, University of Tokyo, Japan.
Honda Z
Nakamura M
Shimizu T
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Źródło:
European journal of biochemistry [Eur J Biochem] 1994 Apr 01; Vol. 221 (1), pp. 211-8.
Typ publikacji:
Comparative Study; Journal Article
MeSH Terms:
Cloning, Molecular*
Gene Expression*
Receptors, Cell Surface*
Receptors, G-Protein-Coupled*
DNA, Complementary/*genetics
Platelet Membrane Glycoproteins/*genetics
Amino Acid Sequence ; Animals ; Base Sequence ; Blotting, Northern ; DNA, Complementary/analysis ; DNA, Complementary/isolation & purification ; Female ; Gene Transfer Techniques ; Guinea Pigs ; Humans ; Introns ; Molecular Sequence Data ; Oocytes/metabolism ; Protein Biosynthesis ; RNA, Messenger/analysis ; Rats ; Restriction Mapping ; Spleen/chemistry ; Tissue Distribution ; Xenopus
Czasopismo naukowe
Tytuł:
Domain B protruding at the third beta strand of the alpha/beta barrel in barley alpha-amylase confers distinct isozyme-specific properties.
Autorzy:
Rodenburg KW; Carlsberg Laboratory, Department of Chemistry, Copenhagen, Denmark.
Juge N
Guo XJ
Søgaard M
Chaix JC
Svensson B
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Źródło:
European journal of biochemistry [Eur J Biochem] 1994 Apr 01; Vol. 221 (1), pp. 277-84.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't
MeSH Terms:
Hordeum/*enzymology
Isoenzymes/*chemistry
alpha-Amylases/*chemistry
Acarbose ; Amino Acid Sequence ; Calcium Chloride/pharmacology ; DNA, Complementary/genetics ; Enzyme Stability ; Gene Transfer Techniques ; Hydrogen-Ion Concentration ; Isoenzymes/antagonists & inhibitors ; Isoenzymes/genetics ; Molecular Sequence Data ; Protein Structure, Secondary ; Recombinant Fusion Proteins/biosynthesis ; Recombinant Fusion Proteins/chemistry ; Saccharomyces cerevisiae/genetics ; Substrate Specificity ; Subtilisins/antagonists & inhibitors ; Trisaccharides/pharmacology ; alpha-Amylases/antagonists & inhibitors ; alpha-Amylases/genetics
Czasopismo naukowe
Tytuł:
Inactivation of antibiotics and the dissemination of resistance genes.
Autorzy:
Davies J; Department of Microbiology and Immunology, University of British Columbia, Vancouver, Canada.
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Źródło:
Science (New York, N.Y.) [Science] 1994 Apr 15; Vol. 264 (5157), pp. 375-82.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't; Review
MeSH Terms:
Genes, Bacterial*
R Factors*
Anti-Bacterial Agents/*antagonists & inhibitors
Drug Resistance, Microbial/*genetics
Amino Acid Sequence ; Aminoglycosides ; Anti-Bacterial Agents/pharmacology ; Chloramphenicol O-Acetyltransferase/genetics ; Chloramphenicol O-Acetyltransferase/metabolism ; Gene Transfer Techniques ; Molecular Sequence Data ; Mutation ; Recombination, Genetic ; beta-Lactamases/genetics ; beta-Lactamases/metabolism ; beta-Lactams
Czasopismo naukowe
Tytuł:
Gene transfer to spark a failing heart.
Autorzy:
Seachrist L
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Źródło:
Science (New York, N.Y.) [Science] 1994 Apr 22; Vol. 264 (5158), pp. 507-8.
Typ publikacji:
Comment; News
MeSH Terms:
Genetic Therapy*
Myocardial Contraction*
Heart/*physiology
Heart Failure/*therapy
Receptors, Adrenergic, beta/*genetics
Animals ; Gene Transfer Techniques ; Humans ; Mice ; Mice, Transgenic ; Receptors, Adrenergic, beta/physiology
Periodyk
Tytuł:
Enhanced myocardial function in transgenic mice overexpressing the beta 2-adrenergic receptor.
Autorzy:
Milano CA; Department of Surgery, Duke University Medical Center, Durham, NC 27710.
Allen LF
Rockman HA
Dolber PC
McMinn TR
Chien KR
Johnson TD
Bond RA
Lefkowitz RJ
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Źródło:
Science (New York, N.Y.) [Science] 1994 Apr 22; Vol. 264 (5158), pp. 582-6.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
MeSH Terms:
Myocardial Contraction*
Ventricular Function, Left*
Adenylyl Cyclases/*metabolism
Myocardium/*metabolism
Receptors, Adrenergic, beta/*genetics
Animals ; Gene Transfer Techniques ; Genetic Therapy ; Heart Failure/physiopathology ; Heart Failure/therapy ; Heart Rate ; Humans ; Isoproterenol/pharmacology ; Mice ; Mice, Transgenic ; Myosins/genetics ; Phenotype ; Promoter Regions, Genetic ; Receptors, Adrenergic, beta/biosynthesis ; Receptors, Adrenergic, beta/physiology
Czasopismo naukowe
Tytuł:
Inhibition of hepatic chylomicron remnant uptake by gene transfer of a receptor antagonist.
Autorzy:
Willnow TE; Department of Molecular Genetics, University of Texas Southwestern Medical Center, Dallas 75235.
Sheng Z
Ishibashi S
Herz J
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Źródło:
Science (New York, N.Y.) [Science] 1994 Jun 03; Vol. 264 (5164), pp. 1471-4.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
MeSH Terms:
Apolipoproteins B/*metabolism
Carrier Proteins/*physiology
Chylomicrons/*metabolism
Glycoproteins/*physiology
Liver/*metabolism
Receptors, Immunologic/*metabolism
Adenoviridae/genetics ; Animals ; Apolipoprotein B-48 ; Carrier Proteins/genetics ; Cholesterol/blood ; Chylomicrons/blood ; Gene Transfer Techniques ; Genetic Vectors ; Glycoproteins/genetics ; LDL-Receptor Related Protein-Associated Protein ; Low Density Lipoprotein Receptor-Related Protein-1 ; Male ; Mice ; Mice, Inbred C57BL ; Receptors, Immunologic/antagonists & inhibitors ; Receptors, LDL/metabolism ; Triglycerides/blood ; alpha-Macroglobulins/metabolism
Czasopismo naukowe

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