- Tytuł:
- Enzyme Replacement Therapy for FABRY Disease: Possible Strategies to Improve Its Efficacy.
- Autorzy:
- Źródło:
- International journal of molecular sciences [Int J Mol Sci] 2023 Feb 25; Vol. 24 (5). Date of Electronic Publication: 2023 Feb 25.
- Typ publikacji:
- Journal Article
- MeSH Terms:
-
Fabry Disease*/metabolism
Humans ; alpha-Galactosidase/metabolism ; Enzyme Replacement Therapy/methods ;Isoenzymes /therapeutic use ; Recombinant Proteins/therapeutic use
Czasopismo naukowe