- Tytuł:
- The LORIS MyeliNeuroGene rare disease database for natural history studies and clinical trial readiness.
- Autorzy:
- Źródło:
- Orphanet journal of rare diseases [Orphanet J Rare Dis] 2021 Jul 23; Vol. 16 (1), pp. 328. Date of Electronic Publication: 2021 Jul 23.
- Typ publikacji:
- Journal Article; Research Support, Non-U.S. Gov't
- MeSH Terms:
-
Quality of Life*
Rare Diseases*/genetics
Databases, Factual ; Female ; Humans ; Parents ; Pregnancy ; United States
Czasopismo naukowe