Development of a porcine model of phenylketonuria with a humanized R408W mutation for gene editing.
Autorzy:
KaiserRA; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America.; Midwest Fetal Care Center, Children's Hospitals and Clinics of Minnesota, Minneapolis, Minnesota, United States of America. Carlson DF; Recombinetics, Inc., St. Paul, Minnesota, United States of America. Allen KL; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America. Webster DA; Recombinetics, Inc., St. Paul, Minnesota, United States of America. VanLith CJ; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America. Nicolas CT; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America.; Faculty of Medicine, University of Barcelona, Barcelona, Spain. Hillin LG; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America. Yu Y; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America. Kaiser CW; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America. Wahoff WR; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America. Hickey RD; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America.; Department of Molecular Medicine, Mayo Clinic, Rochester, Minnesota, United States of America. Watson AL; Recombinetics, Inc., St. Paul, Minnesota, United States of America. Winn SR; Department of Molecular and Medical Genetics, Oregon Health & Science University, Portland, Oregon, United States of America. Thöny B; Department of Pediatrics, University of Zurich, Zurich, Switzerland. Kern DR; Recombinetics, Inc., St. Paul, Minnesota, United States of America. Harding CO; Department of Molecular and Medical Genetics, Oregon Health & Science University, Portland, Oregon, United States of America. Lillegard JB; Department of Surgery, Mayo Clinic, Rochester, Minnesota, United States of America.; Midwest Fetal Care Center, Children's Hospitals and Clinics of Minnesota, Minneapolis, Minnesota, United States of America.; Pediatric Surgical Associates, Minneapolis, Minnesota, United States of America.
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Źródło:
PloS one [PLoS One] 2021 Jan 25; Vol. 16 (1), pp. e0245831. Date of Electronic Publication: 2021 Jan 25 (Print Publication: 2021).
Typ publikacji:
Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
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