Efficacy and safety of givosiran for acute hepatic porphyria: 24-month interim analysis of the randomized phase 3 ENVISION study.
Autorzy:
Ventura P; Department of Surgical and Medical Sciences for Children and Adults, Internal Medicine Unit, University of Modena and Reggio Emilia, Modena, Italy. Bonkovsky HL; Section on Gastroenterology and Hepatology, Wake Forest University/North Carolina Baptist Medical Center, Winston-Salem, NC, USA. Gouya L; Centre Français des Porphyries, Paris, France. Aguilera-Peiró P; Hospital Clinic Barcelona, Barcelona, Spain. Montgomery Bissell D; UCSF Liver Center and Porphyria Center, University of California, San Francisco, CA, USA. Stein PE; King's College Hospital, London, UK. Balwani M; Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, USA. Anderson DKE; University of Texas Medical Branch, Galveston, TX, USA. Parker C; University of Utah, Salt Lake City, UT, USA. KuterDJ; Center for Hematology, Massachusetts General Hospital, Boston, MA, USA. Monroy S; Instituto Nacional de Pediatría, Mexico City, Mexico. Oh J; Konkuk University Medical Center, Seoul, South Korea. Ritchie B; University of Alberta Hospital, Edmonton, Canada. Ko JJ; Alnylam Pharmaceuticals, Cambridge, MA, USA. Hua Z; Alnylam Pharmaceuticals, Cambridge, MA, USA. Sweetser MT; Alnylam Pharmaceuticals, Cambridge, MA, USA. Sardh E; Porphyria Centre Sweden, Centre for Inherited Metabolic Diseases, Karolinska Institutet, Karolinska University Hospital, Stockholm, Sweden.
Quantitative analysis of desmopressin (DDAVP) response in adult patients with type 1 von Willebrand disease.
Autorzy:
Guddati AK; Division of Hematology and Oncology, Georgia Cancer Center, Augusta University, Augusta, Georgia. Rosovsky RP; Division of Hematology, Harvard Medical School, Massachusetts General Hospital, Boston, Massachusetts. Van Cott EM; Department of Pathology, Harvard Medical School, Massachusetts General Hospital, Boston, Massachusetts. KuterDJ; Division of Hematology, Harvard Medical School, Massachusetts General Hospital, Boston, Massachusetts.
Ta witryna wykorzystuje pliki cookies do przechowywania informacji na Twoim komputerze. Pliki cookies stosujemy w celu świadczenia usług na najwyższym poziomie, w tym w sposób dostosowany do indywidualnych potrzeb. Korzystanie z witryny bez zmiany ustawień dotyczących cookies oznacza, że będą one zamieszczane w Twoim komputerze. W każdym momencie możesz dokonać zmiany ustawień dotyczących cookies
