- Tytuł:
- Molecular therapeutic strategies for spinal muscular atrophies: current and future clinical trials.
- Autorzy:
- Źródło:
- Clinical therapeutics [Clin Ther] 2014 Jan 01; Vol. 36 (1), pp. 128-40. Date of Electronic Publication: 2013 Dec 17.
- Typ publikacji:
- Journal Article; Research Support, Non-U.S. Gov't; Review; Systematic Review
- MeSH Terms:
-
Genetic Therapy*
Muscular Atrophy, Spinal/*genetics
Muscular Atrophy, Spinal/*therapy
Survival of Motor Neuron 1 Protein/*genetics
Clinical Trials as Topic ; Humans ; Molecular Targeted Therapy ; Muscular Atrophy, Spinal/drug therapy ; Survival of Motor Neuron 2 Protein/genetics
Czasopismo naukowe