- Tytuł:
-
Splice-Modulating
Antisense Oligonucleotides as Therapeutics for Inherited Metabolic Diseases. - Autorzy:
- Źródło:
- BioDrugs : clinical immunotherapeutics, biopharmaceuticals and gene therapy [BioDrugs] 2024 Mar; Vol. 38 (2), pp. 177-203. Date of Electronic Publication: 2024 Jan 22.
- Typ publikacji:
- Review; Journal Article
- MeSH Terms:
-
Oligonucleotides ,Antisense */therapeutic useOligonucleotides ,Antisense */pharmacology
Metabolic Diseases*/drug therapy
Metabolic Diseases*/genetics
United States ; Humans ;Oligonucleotides /therapeutic use
Czasopismo naukowe