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Wyszukujesz frazę ""Oskoui, Maryam"" wg kryterium: Autor


Tytuł:
Two-year efficacy and safety of risdiplam in patients with type 2 or non-ambulant type 3 spinal muscular atrophy (SMA)
Autorzy:
Oskoui, MaryamAff1, IDs00415023115601_cor1
Day, John W.
Deconinck, NicolasAff3, Aff4
Mazzone, Elena S.
Nascimento, Andres
Saito, Kayoko
Vuillerot, CaroleAff8, Aff9
Baranello, GiovanniAff10, Aff11
Goemans, Nathalie
Kirschner, Janbernd
Kostera-Pruszczyk, Anna
Servais, LaurentAff15, Aff16, Aff17
Papp, Gergely
Gorni, Ksenija
Kletzl, Heidemarie
Martin, Carmen
McIver, Tammy
Scalco, Renata S.
Staunton, Hannah
Yeung, Wai Yin
Fontoura, Paulo
Mercuri, Eugenio
Pokaż więcej
Źródło:
Journal of Neurology. 270(5):2531-2546
Czasopismo naukowe
Tytuł:
Paper I: Heterogeneous use of registry data for participant identification and primary outcome ascertainment is found in registry-based randomized controlled trials: A scoping review
Autorzy:
Baba, Ami
Tay, Joanne
Sammy, Adrian
Douglas, William A.
Goren, Katherine
Krause, Karolin R.
Howie, Alison H.
Little, Julian
Oskoui, Maryam
Taljaard, Monica
Thombs, Brett D.
Potter, Beth K.
Butcher, Nancy J.
Offringa, Martin
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Źródło:
In Journal of Clinical Epidemiology July 2023 159:289-299
Czasopismo naukowe
Tytuł:
Paper II: thematic framework analysis of registry-based randomized controlled trials provided insights for designing trial ready registries
Autorzy:
Krause, Karolin R.
Tay, Joanne
Douglas, William A.
Sammy, Adrian
Baba, Ami
Goren, Katherine
Thombs, Brett D.
Howie, Alison H.
Oskoui, Maryam
Frøbert, Ole
Trakadis, Yannis
Little, Julian
Potter, Beth K.
Butcher, Nancy J.
Offringa, Martin
Pokaż więcej
Źródło:
In Journal of Clinical Epidemiology July 2023 159:330-343
Czasopismo naukowe
Tytuł:
Correction to: Two‑year efficacy and safety of risdiplam in patients with type 2 or non‑ambulant type 3 spinal muscular atrophy (SMA)
Autorzy:
Oskoui, MaryamAff1, IDs00415023116586_cor1
Day, John W.
Deconinck, NicolasAff3, Aff4
Mazzone, Elena S.
Nascimento, Andres
Saito, Kayoko
Vuillerot, CaroleAff8, Aff9
Baranello, GiovanniAff10, Aff11
Goemans, Nathalie
Kirschner, Janbernd
Kostera-Pruszczyk, Anna
Servais, LaurentAff15, Aff16, Aff17
Papp, Gergely
Gorni, Ksenija
Kletzl, Heidemarie
Martin, Carmen
McIver, Tammy
Scalco, Renata S.
Staunton, Hannah
Yeung, Wai Yin
Fontoura, Paulo
Mercuri, Eugenio
Pokaż więcej
Źródło:
Journal of Neurology. 270(5):2547-2549
Czasopismo naukowe
Tytuł:
Safety and efficacy of once-daily risdiplam in type 2 and non-ambulant type 3 spinal muscular atrophy (SUNFISH part 2): a phase 3, double-blind, randomised, placebo-controlled trial
Autorzy:
Volpe, Joseph J.
Posner, John
Kellner, Ulrich
Quinlivan, Rosaline
Daron, Aurore
Delstanche, Stéphanie
Bruninx, Romain
Dal Farra, Fabian
Schneider, Olivier
Deconinck, Nicolas
Balikova, Irina
Delbeke, Patricia
Joniau, Inge
Tahon, Valentine
Wittevrongel, Sylvia
De Vos, Elke
Goemans, Nathalie
Casteels, Ingele
De Waele, Liesbeth
Cassiman, Catherine
Prové, Lies
Kinoo, David
Vancampenhout, Lisa
Van Den Hauwe, Marleen
Van Impe, Annelies
Prufer de Queiroz Campos Araujo, Alexandra
Chacon Pereira, Aline
Nardes, Flávia
Haefeli, Lorena
Rossetto, Julia
Ferreira Rebel, Marcos
Almeida Pereira, Jaqueline
Campbell, Craig
Sharan, Sapna
McDonald, Wendy
Scholtes, Cheryl
Mah, Jean
Sframeli, Maria
Chiu, Angela
Hagel, Jane
Oskoui, Maryam
Beneish, Raquel
Cariou-Palmer, Gaela
Pham, Connie
Toffoli, Daniela
Arpin, Stephanie
Turgeon Desilets, Sarah
Wang, Yi
Hu, Chaoping
Huan, Jianfeng
Qian, Chen
Shen, Li
Xiao, Ying
Zhou, Zhenxuan
Li, Hui
Wang, Sujuan
Xiong, Hui
Chang, Xingzhi
Dong, Hui
Liu, Ying
Sang, Tian
Wei, Cuijie
Wen, Jing
Cao, Yiwen
Ly, Xingyao
Zhao, Jingjing
Li, Wenzhu
Qin, Lun
Barisic, Nina
Galiot Delic, Martina
Ivkic, Petra Kristina
Vukojevic, Nenad
Kern, Ivana
Najdanovic, Boris
Skugor, Marin
Servais, Laurent
Boespflug-Tanguy, Odile
Gidaro, Teresa
Seferian, Andreea
De Lucia, Silvana
Barreau, Emmanuel
Mnafek, Nabila
Momtchilova, Marta Milkova
Peche, Helene
Valherie, Carole
Grange, Allison
Lilien, Charlotte
Milascevic, Darko
Tachibana, Shotaro
Ravelli, Claudia
Cardas, Ruxandra
Taytard, Jessica
Aubertin, Guillaume
Vanden Brande, Laure
Davion, Jean-Baptiste
Coopman, Stephanie
Bouacha, Ikram
Debruyne, Philippe
Defoort, Sabine
Derlyn, Gilles
Leroy, Florian
Danjoux, Loïc
Guilbaud, Julie
Desguerre, Isabelle
Barnérias, Christine
Semeraro, Michaela
Bremond-Gignac, Dominique
Bruere, Lenaic
Rateaux, Maxence
Deladrière, Élodie
Germa, Virginie
Pereon, Yann
Mercie, Sandra
Billaud, Fanny
Le Goff, Lucie
Letellier, Guy
Vuillerot, Carole
Portefaix, Aurélie
De-Montferrand, Camille
Le-Goff, Laure
Fontaine, Stephanie
Saidi, Manel
Bouzid, Nabil
Barriere, Aurélie
Tinat, Marie
Kirschner, Janbernd
Dreesbach, Michelle
Lagréze, Wolf
Michaelis, Bettina
Molnar, Fanni
Seger, Dorina
Vogt, Sibylle
Bertini, Enrico
D'Amico, Adele
Petroni, Sergio
Bonetti, Anna Maria
Carlesi, Adelina
Mizzoni, Irene
Bruno, Claudio
Priolo, Enrico
Rao, Giuseppe
Morando, Simone
Tacchetti, Paola
Zuffi, Ambra
Comi, Giacomo Pietro
Brusa, Roberta
Corti, Stefania
Daniele, Velardo
Govoni, Alessandra
Magri, Francesca
Minorini, Valeria
Osnaghi, Silvia Gabriella
Abbati, Francesca
Fassini, Federica
Foa, Michaela
Lopopolo, Amaqlia
Meneri, Megi
Zoppas, Francesca
Parente, Valeria
Baranello, Giovanni
Masson, Riccardo
Bianchi Marzoli, Stefania
Santarsiero, Diletta
Garcia Sierra, Myriam
Tremolada, Gemma
Arnoldi, Maria Teresa
Vigano, Marta
Zanin, Riccardo
Mercuri, Eugenio
Antonaci, Laura
de Sanctis, Roberto
Pane, Marika
Pera, Maria Carmela
Amorelli, Giulia Maria
Barresi, Costanza
D'Amico, Gugliemo
Orazi, Lorenzo
Coratti, Giorgia
Haginoya, Kazuhiro
Kato, Atsuko
Morishita, Yuko
Kira, Ryutaro
Akiyama, Kiyomu
Goto, Miwako
Mori, Yujiro
Okamoto, Misato
Tsutsui, Saki
Takatsuji, Yuta
Tanaka, Aya
Komaki, Hirofumi
Omori, Miina
Suzuki, Ippei
Takeuchi, Mizuki
Todoroki, Daisuke
Watanabe, Seji
Matsubayashi, Tomoko
Inakazu, Emi
Nagura, Hiroe
Suzuki, Akira
Usui, Manami
Ishikawa, Nobutsune
Harada, Yousuke
Fudeyasu, Kenishi
Hirata, Kazuhiko
Michiue, Kana
Ueda, Kazuyuki
Saito, Kayoko
Fujitani, Junko
Arakawa, Reiko
Takano, Kozue
Yashiro, Shigeko
Seki, Maiko
Sano, Nozomi
Fukuyama, Koji
Matsumoto, Yuki
Miyazaki, Hirofumi
Shibata, Minoru
Kobayashi, Kyoko
Nakamura, Yukie
Takeshima, Yasuhiro
Kuma, Moe
Kostera-Pruszczyk, Anna
Fraczek, Anna
Jedrzejowska, Maria
Lusakowska, Anna
Czeszyk-Piotrowicz, Agnieszka
Hautz, Wojciech
Rakusiewicz, Klaudia
Burlewicz, Malgorzata
Gierlak-Wojcicka, Zuzanna
Kepa, Malwina
Sikorski, Adam
Sobieraj, Marcin
Mazurkiewicz-Beldzinska, Maria
Lemska, Anna
Modrzejewska, Sandra
Koberda, Mateusz
Stodolska-Koberda, Urszula
Waskowska, Agnieszka
Kolendo, Jagoda
Sobierajska-Rek, Agnieszka
Steinborn, Barbara
Dalz, Magdalena
Grabowska, Julia
Hajduk, Wojciech
Janasiewicz-Karachitos, Justyna
Klimas, Monika
Stopa, Marcin
Gajewska, Ewa
Pusz, Beata
Vlodavets, Dmitry
Melnik, Evgenia
Leppenen, Natalya
Yupatova, Nataliya
Monakhova, Anastasya
Papina, Yulia
Shidlovsckaia, Olga
Milic Rasic, Vedrana
Brankovic, Vesna
Kosac, Ana
Djokic, Olivera
Jakšic, Vesna
Pepic, Ana
Martinovic, Jelena
Munell Casadesus, Francina
Tizzano, Eduardo
Martín Begué, Nieves
Wolley Dod, Charlotte
Subira, Olaia
Planas Pascual, Bernat
Toro Tamargo, Esther
Madruga Garrido, Marcos
Medina Romero, José David
Salinas, Marta Peña
Nascimento Osorio, Andrés
Díaz Cortés, Ana
Jiménez Gañan, Enrique
Suh, Simone Dowon
Medina Cantillo, Julita
Moya, Obdulia
Padros, Nuria
Urraca, Sandra Roca
Valdivia, Hugo Gonzalez
Pascual Pascual, Samuel
de Manuel, Sofía
Martin, Susana Noval
Burnham, Paul
Espinosa, Sandra
Moreno, Mercedes Martinez
Topaloglu, Haluk
Oncel, Ibrahim
Eroglu Ertugru, Nesibe
Konuskan, Bahadir
Eldem, Bora
Kadayifçilar, Sibel
Alemdaroglu, Ipek
Karaduman, Aynur Ayse
Yilmaz, Oznur Tunca
Bilgin, Neslihan
Sari, Seher
Chiriboga, Claudia
Lee, John J.
Rome-Martin, Donnielle
Day, John W.
Beres, Shannon
Duong, Tina
Gee, Richard
Dunaway Young, Sally
Fuerst-Recktenwald, Sabine
Marquet, Anne
Muelhardt, Nicoletta
Trundell, Dylan
Mazzone, Elena S
Nascimento, Andres
Gerber, Marianne
Gorni, Ksenija
Khwaja, Omar
Kletzl, Heidemarie
Scalco, Renata S
Staunton, Hannah
Yeung, Wai Yin
Martin, Carmen
Fontoura, Paulo
Day, John W
Pokaż więcej
Źródło:
In The Lancet Neurology January 2022 21(1):42-52
Czasopismo naukowe
Tytuł:
Newborn screening programs for spinal muscular atrophy worldwide: Where we stand and where to go
Autorzy:
Adoukonou, Thierry
Aryani, Omid
Barisic, Nina
Bashiri, Fahad
Bastaki, Laila
Benitto, Afaf
Omran, Tawfeg Ben
Bernert, Guenther
Bertini, Enrico
Borde, Patricia
Born, Peter
Boustani, Rose-Mary
Butoianu, Nina
Castiglioni, Claudia
Catibusic, Feriha
Chan, Sophelia
Chien, Yin Hsiu
Christodoulou, Kyproula
Dejsuphong, Donniphat
Farrar, Michelle
Filip, Duma
Goemans, Nathalie
Guinhouya, Kokou
Haberlova, Jana
Hadzsiev, Kinga
Hovhannesyan, Kristine
Isohanni, Pirjo
Radovic, Nelica Ivanovic
Jacquier, David
Jalloh, Alusine
Jedrzejowska, Maria
Kandawasvika, Gwen
Kaputu, Celestin
Kawatu, Nfwama
Kernohan, Kristin
Kirschner, Jan
Klink, Barbara
Kodsy, Sherry
Kouame-Assouan, Ange-Eric
Kravljanac, Ruzica
Kreile, Madara
Litvinenko, Ivan
McMillan, Hugh
Mesa, Sandra
Mohamed, Inaam
Kanzoska, Liljana Muaremoska
Nevo, Yoram
Nguefack, Seraphin
Nkole, Kafula
O'Grady, Gina
O'Rourke, Declan
Oskoui, Maryam
Piazzon, Flavia
Poddighe, Dimitri
Prasauskiene, Audrone
Prieto, Juan
Rasmussen, Magnhild
Razafindrasata, Santara
Saha, Narayan
Saito, Kayoko
Sakadi, Foksouna
Sangare, Modibo
Schroth, Mary
Shalkevich, Leanid
Shatillo, Andriy
Suthar, Renu
Szabo, Lena
Tatishvili, Nana
Tazir, Meriem
Tizzano, Eduardo
Topaloglu, Haluk
Tulinius, Mar
van der Pol, Ludo
Vazquez, Gabriel
Vlodavets, Dimitry
Wanigasinghe, Jithangi
Wilmshurst, Jo
Xiong, Hui
Zafeiriou, Dimitrios
Zamba, Eleni
Dangouloff, Tamara
Vrščaj, Eva
Servais, Laurent
Osredkar, Damjan
Pokaż więcej
Źródło:
In Neuromuscular Disorders June 2021 31(6):574-582
Czasopismo naukowe
Tytuł:
Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study
Autorzy:
Rudnicki, Stacy A.
Andrews, Jinsy A.Aff1, Aff2
Duong, Tina
Cockroft, Bettina M.Aff1, Aff4
Malik, Fady I.
Meng, Lisa
Wei, Jenny
Wolff, Andrew A.
Genge, Angela
Johnson, Nicholas E.Aff6, Aff7
Tesi-Rocha, Carolina
Connolly, Anne M.Aff8, Aff9
Darras, Basil T.
Felice, Kevin
Finkel, Richard S.Aff12, Aff13
Shieh, Perry B.
Mah, Jean K.
Statland, Jeffrey
Campbell, Craig
Habib, Ali A.
Kuntz, Nancy L.
Oskoui, Maryam
Day, John W.
Pokaż więcej
Źródło:
Neurotherapeutics: The Journal of the American Society for Experimental Neurotherapeutics. 18(2):1127-1136
Czasopismo naukowe

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