- Tytuł:
- Trial in progress: An open-label study (AT1001-025) to evaluate the safety and pharmacokinetics of migalastat in patients with Fabry disease and amenable GLA variants and severe renal impairment or end-stage renal disease treated with hemodialysis
- Autorzy:
- Źródło:
- In Molecular Genetics and Metabolism February 2024 141(2)
Czasopismo naukowe