- Tytuł:
- Base editing rescue of spinal muscular atrophy in cells and in mice.
- Autorzy:
- Źródło:
- Science (New York, N.Y.) [Science] 2023 Apr 21; Vol. 380 (6642), pp. eadg6518. Date of Electronic Publication: 2023 Apr 14.
- Typ publikacji:
- Journal Article
- MeSH Terms:
-
Gene Editing*
Muscular Atrophy, Spinal*/genetics
Muscular Atrophy, Spinal*/therapySurvival ofMotor Neuron 1 Protein */geneticsSurvival ofMotor Neuron 2Protein */genetics
Animals ; Mice ; Fibroblasts/metabolism ;Motor Neurons/metabolism
Czasopismo naukowe