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Wyszukujesz frazę ""compassionate use"" wg kryterium: Temat


Tytuł:
Efficacy and safety of compassionate use for rare diseases: a scoping review from 1991 to 2022.
Autorzy:
Wu J; Department of Pharmacy and State Key Laboratory of Complex Severe and Rare Disease, Peking Union Medical College Hospital (Dongdan Campus), Chinese Academy of Medical Sciences and Peking Union Medical College, No.1 Shuaifuyuan Wangfujing Dongcheng District, Beijing, 100730, China.
Yang Y; Department of Pharmacy and State Key Laboratory of Complex Severe and Rare Disease, Peking Union Medical College Hospital (Dongdan Campus), Chinese Academy of Medical Sciences and Peking Union Medical College, No.1 Shuaifuyuan Wangfujing Dongcheng District, Beijing, 100730, China.
Yu J; Department of Pharmacy and State Key Laboratory of Complex Severe and Rare Disease, Peking Union Medical College Hospital (Dongdan Campus), Chinese Academy of Medical Sciences and Peking Union Medical College, No.1 Shuaifuyuan Wangfujing Dongcheng District, Beijing, 100730, China.
Qiao L; Department of Pharmacy and State Key Laboratory of Complex Severe and Rare Disease, Peking Union Medical College Hospital (Dongdan Campus), Chinese Academy of Medical Sciences and Peking Union Medical College, No.1 Shuaifuyuan Wangfujing Dongcheng District, Beijing, 100730, China.; State Key Laboratory of Bioactive Substance and Function of Natural Medicines, Institute of Material Medica, Chinese Academy of Medical Sciences and Peking Union Medical College, Beijing, 100050, China.
Zuo W; Department of Pharmacy and State Key Laboratory of Complex Severe and Rare Disease, Peking Union Medical College Hospital (Dongdan Campus), Chinese Academy of Medical Sciences and Peking Union Medical College, No.1 Shuaifuyuan Wangfujing Dongcheng District, Beijing, 100730, China. .
Zhang B; Department of Pharmacy and State Key Laboratory of Complex Severe and Rare Disease, Peking Union Medical College Hospital (Dongdan Campus), Chinese Academy of Medical Sciences and Peking Union Medical College, No.1 Shuaifuyuan Wangfujing Dongcheng District, Beijing, 100730, China. .
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Źródło:
Orphanet journal of rare diseases [Orphanet J Rare Dis] 2023 Nov 28; Vol. 18 (1), pp. 368. Date of Electronic Publication: 2023 Nov 28.
Typ publikacji:
Journal Article; Review
MeSH Terms:
Compassionate Use Trials*
Neoplasms*/drug therapy
Humans ; Adult ; Drugs, Investigational/adverse effects ; Rare Diseases/drug therapy ; Drug Approval
Czasopismo naukowe
Tytuł:
Real-world treatment outcomes of medicines used in special situations (off-label and compassionate use) in oncology and hematology: A retrospective study from a comprehensive cancer institution.
Autorzy:
Fontanals S; Pharmacy Department, Catalan Institute of Oncology (ICO)-Hospitalet, Institut d'Investigació Biomèdica de Bellvitge (IDIBELL), School of Medicine, Universitat de Barcelona (UB), Barcelona, Spain.
Esteve A; Research Management Unit (Unitat de Gestió de la recerca: UGR), Medical Oncology Department, Catalan Institute of Oncology (ICO), Badalona-Applied Research Group in Oncology (B-ARGO), Germans Trias I Pujol Research Institute (IGTP), Badalona, Spain.
González A; Medical Oncology Department, Catalan Institute of Oncology (ICO), Badalona-Applied Research Group in Oncology (B-ARGO) Germans Trias I Pujol Research Institute (IGTP), Badalona, Spain.
Ibáñez C; Pharmacy Department, Catalan Institute of Oncology (ICO)-Hospitalet, School of Health Sciences, Blanquerna Ramon Llull University, Barcelona, Spain.
Martínez J; Pharmacy Department, Catalan Institute of Oncology (ICO)-Hospitalet, Barcelona, Spain.
Mesía R; Medical Oncology Department, Catalan Institute of Oncology (ICO), Badalona-Applied Research Group in Oncology (B-ARGO) Germans Trias I Pujol Research Institute (IGTP), Badalona, Spain.
Clopés A; Pharmacy Department, Catalan Institute of Oncology (ICO)-Hospitalet, Institut d'Investigació Biomèdica de Bellvitge (IDIBELL), School of Health Sciences, Blanquerna Ramon Llull University, Barcelona, Spain.
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Źródło:
Cancer medicine [Cancer Med] 2023 Aug; Vol. 12 (16), pp. 17112-17125. Date of Electronic Publication: 2023 Jul 26.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't
MeSH Terms:
Compassionate Use Trials*
Neoplasms*/drug therapy
Adult ; Humans ; Female ; Retrospective Studies ; Off-Label Use ; Treatment Outcome
Czasopismo naukowe
Tytuł:
Single-patient expanded access: A primer for pharmacists.
Autorzy:
Smith AJF; Department of Pharmacy Services, Michigan Medicine, Ann Arbor, MI, USA.
Redic KA; Department of Pharmacy Services, Michigan Medicine, Ann Arbor, MI, USA.
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Źródło:
American journal of health-system pharmacy : AJHP : official journal of the American Society of Health-System Pharmacists [Am J Health Syst Pharm] 2022 Nov 22; Vol. 79 (23), pp. 2118-2127.
Typ publikacji:
Journal Article
MeSH Terms:
Pharmacists*
Compassionate Use Trials*
United States ; Humans ; Drugs, Investigational/therapeutic use ; United States Food and Drug Administration ; Therapies, Investigational
Czasopismo naukowe
Tytuł:
[Summary of the conference "Phages and phage therapy: from Félix d'Hérelle to 2.0 phages"].
Autorzy:
Defresne T
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Transliterated Title:
Revue de synthèse de la conférence « Phages et phagothérapie : de Félix d’Hérelle aux phages 2.0 »1.
Źródło:
Virologie (Montrouge, France) [Virologie (Montrouge)] 2023 Aug 01; Vol. 27 (4), pp. 219-224.
Typ publikacji:
English Abstract; Journal Article
MeSH Terms:
Bacteriophages*
Phage Therapy*
Humans ; Bacteria ; Anti-Bacterial Agents ; Compassionate Use Trials
Czasopismo naukowe
Tytuł:
Structural violence and the need for compassionate use of methadone in Mexico.
Autorzy:
Romero-Mendoza M; Instituto Nacional de Psiquiatría Ramón de La Fuente Muñiz, Camino a Xochimilco 101, Col, San Lorenzo Huipulco, CDMX, 144370, Tlalpan, Mexico City, Mexico. .
Peláez-Ballestas I; Hospital General de México Dr. Eduardo Liceaga, Dr. Balmis 148, Col. Doctores, CDMX, 06720, Cuauhtémoc, Mexico City, Mexico.
Almanza-Avendaño AM; Facultad de Ciencias Humanas, Universidad Autónoma de Baja California, Calz. Castellón S/N, Esperanza Conjunto Urbano, 21350, Mexicali, BC, Mexico.
Figueroa E; Clínica Integral de Tratamiento Contra Las Adicciones, Adolfo Prieto 1338, Col. Del Valle, Benito Juárez, CDMX, 03100, Mexico City, Mexico.
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Źródło:
BMC public health [BMC Public Health] 2022 Mar 29; Vol. 22 (1), pp. 606. Date of Electronic Publication: 2022 Mar 29.
Typ publikacji:
Journal Article
MeSH Terms:
Compassionate Use Trials*
Heroin Dependence*/drug therapy
Heroin Dependence*/epidemiology
Heroin Dependence*/psychology
Adult ; Female ; Humans ; Male ; Methadone/therapeutic use ; Mexico/epidemiology ; Middle Aged ; Violence
Czasopismo naukowe
Tytuł:
The economic impact of compassionate use of medicines.
Autorzy:
Jommi C; Centre for Research on Health and Social Care Management, SDA Bocconi School of Management, CERGAS, Bocconi University, Via Sarfatti 25, 20136, Milano, MI, Italy. .
Pantellini F; ROCHE Spa, Viale GB Stucchi 110, MB, 20900, Monza, Italy.
Stagi L; ROCHE Spa, Viale GB Stucchi 110, MB, 20900, Monza, Italy.
Verykiou M; Centre for Research on Health and Social Care Management, SDA Bocconi School of Management, CERGAS, Bocconi University, Via Sarfatti 25, 20136, Milano, MI, Italy.
Cavazza M; Centre for Research on Health and Social Care Management, SDA Bocconi School of Management, CERGAS, Bocconi University, Via Sarfatti 25, 20136, Milano, MI, Italy.
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Źródło:
BMC health services research [BMC Health Serv Res] 2021 Dec 04; Vol. 21 (1), pp. 1303. Date of Electronic Publication: 2021 Dec 04.
Typ publikacji:
Journal Article
MeSH Terms:
Compassionate Use Trials*
Multiple Sclerosis*
Cost-Benefit Analysis ; Humans ; Italy ; State Medicine
Czasopismo naukowe
Tytuł:
Oncologists' reflections on patient rights and access to compassionate use drugs: A qualitative interview study from an academic cancer center.
Autorzy:
Stout J; Mayo Clinic Alix School of Medicine, Rochester, MN, United States of America.; Biomedical Ethics Research Program, Mayo Clinic, Rochester, MN, United States of America.
Smith C; UNC Chapel Hill School of Medicine, Chapel-Hill, NC, United States of America.
Buckner J; Department of Oncology, Mayo Clinic, Rochester, MN, United States of America.
Adjei AA; Department of Oncology, Mayo Clinic, Rochester, MN, United States of America.
Wentworth M; Digestive Disease and Surgery Institute, Cleveland Clinic, Cleveland, OH, United States of America.
Tilburt JC; Biomedical Ethics Research Program, Mayo Clinic, Rochester, MN, United States of America.; General Internal Medicine, Mayo Clinic, Scottsdale, AZ, United States of America.
Master Z; Biomedical Ethics Research Program, Mayo Clinic, Rochester, MN, United States of America.; Center for Regenerative Medicine, Mayo Clinic, Rochester, MN, United States of America.
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Źródło:
PloS one [PLoS One] 2021 Dec 17; Vol. 16 (12), pp. e0261478. Date of Electronic Publication: 2021 Dec 17 (Print Publication: 2021).
Typ publikacji:
Journal Article; Research Support, N.I.H., Extramural; Research Support, U.S. Gov't, P.H.S.
MeSH Terms:
Compassionate Use Trials*
Drugs, Investigational*/therapeutic use
Neoplasms*/drug therapy
Oncologists*/psychology
Therapies, Investigational*
Humans ; Drug Approval ; Interviews as Topic ; Motivation ; Patient Rights ; Physician-Patient Relations ; United States
Czasopismo naukowe
Tytuł:
Soliris to Stop Immune-Mediated Death in COVID-19 (SOLID-C19)-A Compassionate-Use Study of Terminal Complement Blockade in Critically Ill Patients with COVID-19-Related Adult Respiratory Distress Syndrome.
Autorzy:
Pitts TC; Hudson Medical, 281 Broadway, 2nd Fl., New York, NY 10007, USA.
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Źródło:
Viruses [Viruses] 2021 Dec 03; Vol. 13 (12). Date of Electronic Publication: 2021 Dec 03.
Typ publikacji:
Journal Article
MeSH Terms:
Antibodies, Monoclonal, Humanized*
Compassionate Use Trials*
Complement System Proteins*
COVID-19/*immunology
COVID-19/*mortality
Adolescent ; Adult ; Aged ; Aged, 80 and over ; Critical Illness ; Female ; Humans ; Male ; Middle Aged ; Pilot Projects ; Respiratory Distress Syndrome ; SARS-CoV-2 ; Young Adult
Czasopismo naukowe
Tytuł:
Compassionate use of ruxolitinib in patients with SARS-Cov-2 infection not on mechanical ventilation: Short-term effects on inflammation and ventilation.
Autorzy:
Mortara A; Department of Clinical Cardiology, Policlinico di Monza, Monza, Italy.
Mazzetti S; Department of Clinical Cardiology, Policlinico di Monza, Monza, Italy.
Margonato D; Department of Clinical Cardiology, Policlinico di Monza, Monza, Italy.; Department of Cardiology, University of Pavia, Pavia, Italy.
Delfino P; Department of Clinical Cardiology, Policlinico di Monza, Monza, Italy.
Bersano C; Department of Clinical Cardiology, Policlinico di Monza, Monza, Italy.
Catagnano F; Department of Clinical Cardiology, Policlinico di Monza, Monza, Italy.; Department of Cardiology, University of Pavia, Pavia, Italy.
Lauriola M; Department of Internal Medicine, Policlinico di Monza, Monza, Italy.
Grosso P; Department of Anaesthesiology and Intensive Care, Policlinico di Monza, Monza, Italy.
Perseghin G; Department of Medicine and Rehabilitation, Policlinico di Monza, Università degli Studi di Milano Bicocca, Monza, Italy.
Ippoliti G; Department of Internal Medicine, Policlinico di Monza, Monza, Italy.
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Źródło:
Clinical and translational science [Clin Transl Sci] 2021 May; Vol. 14 (3), pp. 1062-1068. Date of Electronic Publication: 2021 Jan 27.
Typ publikacji:
Journal Article
MeSH Terms:
Compassionate Use Trials*
SARS-CoV-2*
COVID-19 Drug Treatment*
Anti-Inflammatory Agents/*therapeutic use
Janus Kinase Inhibitors/*therapeutic use
Pyrazoles/*therapeutic use
Respiration/*drug effects
Adult ; Aged ; Aged, 80 and over ; COVID-19/physiopathology ; Female ; Humans ; Male ; Middle Aged ; Nitriles ; Pyrimidines ; Respiration, Artificial
Czasopismo naukowe
Tytuł:
Severe sinus bradycardia associated with Remdesivir in a child with severe SARS-CoV-2 infection.
Autorzy:
Sanchez-Codez MI; Division of Pediatric Infectious Diseases, Puerta del Mar University Hospital, Av. Ana de Viya, 21, 11009, Cadiz, Spain. .
Rodriguez-Gonzalez M; Division of Pediatric Cardiology, Puerta del Mar University Hospital, Cadiz, Spain.
Gutierrez-Rosa I; Department of Pediatrics, Puerta del Mar University Hospital, Cadiz, Spain.
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Źródło:
European journal of pediatrics [Eur J Pediatr] 2021 May; Vol. 180 (5), pp. 1627. Date of Electronic Publication: 2021 Jan 23.
Typ publikacji:
Letter; Comment
MeSH Terms:
Compassionate Use Trials*
COVID-19 Drug Treatment*
Adenosine Monophosphate/analogs & derivatives ; Alanine/analogs & derivatives ; Bradycardia/chemically induced ; Child ; Humans ; SARS-CoV-2
Opinia redakcyjna
Tytuł:
Compassionate use of remdesivir in children with COVID-19.
Autorzy:
Méndez-Echevarría A; Paediatric Infectious Diseases Department, Translational Research Network in Paediatric Infectious Diseases (RITIP), La Paz University Hospital, Paseo de la Castellana 261, 28046, Madrid, Spain. .
Pérez-Martínez A; Paediatric Hemato-Oncology Department, Translational Research in Pediatric Oncology, Hematopoietic Transplantation and Cell Therapy, La Paz University Hospital, La Paz Institute for Health Research (IdiPAZ), Madrid, Spain.
Gonzalez Del Valle L; Pharmacy Department, La Paz University Hospital, Madrid, Spain.
Ara MF; Department of Paediatrics and Neonatology, Quironsalud Madrid University Hospital, Madrid, Spain.
Melendo S; Paediatric Infectious Diseases and Immunodeficiencies Unit, Hospital Universitari Vall d'Hebron (HUVH). Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Ruiz de Valbuena M; Pediatric Pulmunology Unit, La Paz University Hospital, Madrid, Spain.
Vazquez-Martinez JL; Paediatric Intensive Care Unit, Ramon y Cajal Universitary Hospital, Madrid, Spain.
Morales-Martínez A; Paediatric Intensive Care Unit, Universitary Regional Málaga Hospital, Málaga, Spain.
Remesal A; Paediatric Rheumatology Unit, La Paz University Hospital, Madrid, Spain.
Sándor-Bajusz KA; Department of Paediatrics, University of Pécs Medical School, Pécs, Hungary.
Cabañas F; Department of Neonatology, Quironsalud Madrid University Hospital and Biomedical Research Foundation, La Paz University Hospital Madrid, Madrid, Spain.
Calvo C; Paediatric Infectious Diseases Department, Translational Research Network in Paediatric Infectious Diseases (RITIP), La Paz University Hospital, Paseo de la Castellana 261, 28046, Madrid, Spain.
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Źródło:
European journal of pediatrics [Eur J Pediatr] 2021 Apr; Vol. 180 (4), pp. 1317-1322. Date of Electronic Publication: 2020 Nov 16.
Typ publikacji:
Journal Article; Multicenter Study; Observational Study
MeSH Terms:
Compassionate Use Trials*
COVID-19 Drug Treatment*
Adenosine Monophosphate/*analogs & derivatives
Alanine/*analogs & derivatives
Antiviral Agents/*therapeutic use
Adenosine Monophosphate/therapeutic use ; Adolescent ; Alanine/therapeutic use ; Child ; Child, Preschool ; Critical Illness ; Female ; Humans ; Infant ; Male ; Severity of Illness Index ; Spain ; Treatment Outcome
Czasopismo naukowe
Tytuł:
Compassionate use of recombinant human IL-7-hyFc as a salvage treatment for restoring lymphopenia in patients with recurrent glioblastoma.
Autorzy:
Ahn S; Department of Neurosurgery, Seoul St. Mary's Hospital, College of Medicine, The Catholic University of Korea, Seoul, South Korea.
Park JS; Department of Neurosurgery, Seoul St. Mary's Hospital, College of Medicine, The Catholic University of Korea, Seoul, South Korea.
Kim H; Genexine, Inc., Seongnam-si, Gyeonggi-do, South Korea.
Heo M; Genexine, Inc., Seongnam-si, Gyeonggi-do, South Korea.
Sung YC; Genexine, Inc., Seongnam-si, Gyeonggi-do, South Korea.
Jeun SS; Department of Neurosurgery, Seoul St. Mary's Hospital, College of Medicine, The Catholic University of Korea, Seoul, South Korea.
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Źródło:
Cancer medicine [Cancer Med] 2023 Mar; Vol. 12 (6), pp. 6778-6787. Date of Electronic Publication: 2022 Dec 30.
Typ publikacji:
Journal Article
MeSH Terms:
Glioblastoma*/drug therapy
Lymphopenia*/etiology
Brain Neoplasms*
Humans ; Interleukin-7/therapeutic use ; Compassionate Use Trials ; Salvage Therapy/methods ; Neoplasm Recurrence, Local/drug therapy ; Immunologic Factors/therapeutic use
Czasopismo naukowe
Tytuł:
Compassionate use of long-acting cabotegravir plus rilpivirine for people living with HIV-1 in need of parenteral antiretroviral therapy.
Autorzy:
D'Amico R; ViiV Healthcare, Durham, North Carolina, USA.
Cenoz Gomis S; ViiV Healthcare, Madrid, Spain.
Moodley R; ViiV Healthcare, Brentford, UK.
Van Solingen-Ristea R; Janssen Pharmaceutica, Beerse, Belgium.
Baugh B; Janssen Pharmaceutica, Raritan, New Jersey, USA.
Van Landuyt E; Janssen Pharmaceutica, Beerse, Belgium.
Van Eygen V; Janssen Pharmaceutica, Beerse, Belgium.
Min S; ViiV Healthcare, Durham, North Carolina, USA.
Cutrell A; ViiV Healthcare, Durham, North Carolina, USA.
Foster C; Imperial College NHS Healthcare Trust, London, UK.
Chilton D; Guys and St Thomas NHS Healthcare Trust, London, UK.
Allard SD; HIV Reference Center Universitair Ziekenhuis Brussel, Brussels, Belgium.
Ruiter A; ViiV Healthcare, Brentford, UK.
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Źródło:
HIV medicine [HIV Med] 2023 Feb; Vol. 24 (2), pp. 202-211. Date of Electronic Publication: 2022 Aug 09.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't
MeSH Terms:
HIV Infections*/drug therapy
HIV-1*/genetics
Anti-HIV Agents*/pharmacology
Anti-HIV Agents*/therapeutic use
HIV Seropositivity*/drug therapy
Humans ; Rilpivirine/pharmacology ; Rilpivirine/therapeutic use ; Compassionate Use Trials ; Viremia/drug therapy ; Anti-Retroviral Agents/therapeutic use
Czasopismo naukowe
Tytuł:
Response to Open Peer Commentary "Making It Count: Extracting Real World Data from Compassionate Use and Expanded Access Programs".
Autorzy:
Polak TB; Erasmus Medical Center.; Erasmus University Rotterdam.; myTomorrows.
van Rosmalen J; Erasmus Medical Center.
Uyl-De Groot CA; Erasmus University Rotterdam.
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Źródło:
The American journal of bioethics : AJOB [Am J Bioeth] 2020 Nov; Vol. 20 (11), pp. W4-W5.
Typ publikacji:
Letter; Comment
MeSH Terms:
Compassionate Use Trials*
Drugs, Investigational*
Humans ; Research
Opinia redakcyjna
Tytuł:
Making It Count: Extracting Real World Data from Compassionate Use and Expanded Access Programs.
Autorzy:
Rozenberg O; Zvi Meitar Institute for Legal Implications of Emerging Technologies, Interdisciplinary Center Herzliya.
Greenbaum D; Zvi Meitar Institute for Legal Implications of Emerging Technologies, Interdisciplinary Center Herzliya.; Harry Radyzner Law School, Interdisciplinary Center Herzliya.; Molecular Biophysics and Biochemistry, Yale University.
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Źródło:
The American journal of bioethics : AJOB [Am J Bioeth] 2020 Jul; Vol. 20 (7), pp. 89-92.
Typ publikacji:
Journal Article
MeSH Terms:
Compassionate Use Trials*
Drugs, Investigational*
Health Services Accessibility ; Humans ; Research
Czasopismo naukowe
Tytuł:
Oversight of Right-to-Try and Expanded Access Requests for Off-Trial Access to Investigational Drugs.
Autorzy:
Chapman CR; Faculty affiliate of the Division of Medical Ethics in the Department of Population Health in the NYU School of Medicine at NYU Langone Health.
Eckman J; Worked on this article as an intern in the Division of Medical Ethics in the Department of Population Health at NYU School of Medicine at NYU Langone Health and is currently pursuing an MD as well as an MA in bioethics at Emory School of Medicine.
Bateman-House AS; Assistant professor in the Division of Medical Ethics in the Department of Population Health in the NYU School of Medicine at NYU Langone Health.
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Źródło:
Ethics & human research [Ethics Hum Res] 2020 Jan; Vol. 42 (1), pp. 2-13.
Typ publikacji:
Journal Article
MeSH Terms:
Compassionate Use Trials*
Drugs, Investigational*
Research*
Humans ; United States ; United States Food and Drug Administration/legislation & jurisprudence
Czasopismo naukowe
Tytuł:
Current State of Compassionate Phage Therapy.
Autorzy:
McCallin S; Unit of Regenerative Medicine, Department of Musculoskeletal Medicine, Service of Plastic, Reconstructive, & Hand Surgery, University Hospital of Lausanne (CHUV), 1066 Epalignes, Switzerland. .; Swiss Federal Institute of Technology Lausanne (EPFL), 1015 Lausanne, Switzerland. .
Sacher JC; Phage Directory, Atlanta, GA 30303, USA. .
Zheng J; Phage Directory, Atlanta, GA 30303, USA. .
Chan BK; Yale University New Haven, CT 06520, USA. .
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Źródło:
Viruses [Viruses] 2019 Apr 12; Vol. 11 (4). Date of Electronic Publication: 2019 Apr 12.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't; Review
MeSH Terms:
Compassionate Use Trials*
Phage Therapy*
Bacterial Infections/*therapy
Drug Resistance, Multiple, Bacterial ; Humans
Czasopismo naukowe
Tytuł:
Short-term safety results from compassionate use of risdiplam in patients with spinal muscular atrophy in Germany.
Autorzy:
Hahn A; Department of Child Neurology, University of Gießen, Giessen, Germany.
Günther R; Department of Neurology, University Hospital Carl Gustav Carus, Technische Universität Dresden, Dresden, Germany.
Ludolph A; Department of Neurology, University of Ulm, Ulm, Germany.
Schwartz O; Department of Pediatric Neurology, Münster University Hospital, Münster, Germany.
Trollmann R; Division of Pediatric Neurology, Department of Pediatrics, Friedrich-Alexander-Universität Erlangen-Nürnberg, Erlangen, Germany.
Weydt P; Department of Neurodegenerative Diseases and Gerontopsychiatry/Neurology, University of Bonn Medical Center, Bonn, Germany.
Weiler M; Department of Neurology, Heidelberg University Hospital, Heidelberg, Germany.
Neuland K; Roche Pharma AG, Grenzach-Wyhlen, Germany.
Schwaderer MS; Roche Pharma AG, Grenzach-Wyhlen, Germany.
Hagenacker T; Department of Neurology, University Hospital Essen, Essen, Germany. .
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Corporate Authors:
Risdiplam Compassionate Use Program Group
Źródło:
Orphanet journal of rare diseases [Orphanet J Rare Dis] 2022 Jul 19; Vol. 17 (1), pp. 276. Date of Electronic Publication: 2022 Jul 19.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't
MeSH Terms:
Muscular Atrophy, Spinal*/drug therapy
Spinal Muscular Atrophies of Childhood*/drug therapy
Azo Compounds ; Compassionate Use Trials ; Germany ; Humans ; Infant ; Pyrimidines
Czasopismo naukowe
Tytuł:
Zanamivir aqueous solution in severe influenza: A global Compassionate Use Program, 2009-2019.
Autorzy:
Wang-Jairaj J; Clinical Science, R&D, GSK, Brentford, Middlesex, UK.
Miller I; Safety and Medical Governance, R&D Global Medical, GSK, Brentford, Middlesex, UK.
Joshi A; Development Biostatistics, GSK, Bangalore, India.
Jayabalan T; Safety and Medical Governance, R&D Global Medical, GSK, Brentford, Middlesex, UK.
Peppercorn A; Clinical Development, GSK, Boston, Massachusetts, USA.
Zammit-Tabona P; Global Clinical Science and Delivery, R&D, GSK, Collegeville, Pennsylvania, USA.
Oliver A; Global Health R&D, GSK, Brentford, Middlesex, UK.
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Źródło:
Influenza and other respiratory viruses [Influenza Other Respir Viruses] 2022 May; Vol. 16 (3), pp. 542-551. Date of Electronic Publication: 2021 Dec 22.
Typ publikacji:
Journal Article; Research Support, Non-U.S. Gov't
MeSH Terms:
Influenza A Virus, H1N1 Subtype*
Influenza, Human*/drug therapy
Antiviral Agents/adverse effects ; Compassionate Use Trials ; Enzyme Inhibitors/adverse effects ; Humans ; Infant ; Neuraminidase ; Oseltamivir/therapeutic use ; Zanamivir/adverse effects
Czasopismo naukowe
Tytuł:
Clinical Experience of Immunotherapy Treatment: Efficacy and Toxicity Analysis of the Compassionate Use Program of Nivolumab in Patients with Advanced Squamous Cell Non-Small Cell Lung Cancer.
Autorzy:
Krefting F; Department of Medical Oncology, West German Cancer Center, University Hospital Essen, Essen, Germany, .
Basara N; Department of Hematology and Oncology, Malteser Clinic St. Franziskus-Hospital, Flensburg, Germany.
Schütte W; Department of Internal Medicine II, Martha-Maria Hospital Halle-Dölau, Halle, Germany.
Späth-Schwalbe E; Department of Hematology and Oncology, Vivantes Clinic Spandau, Berlin, Germany.
Alt J; Department of Internal Medicine III, Universitätsmedizin Mainz, Mainz, Germany.
Thiel S; Department of Pneumology, Helios Clinic Emil von Behring, Berlin, Germany.
Kimmich M; Department of Pneumology, Clinic Schillerhoehe, Gerlingen, Germany.
Fischer JR; Department of Internal Medicine II, Lungenklinik Löwenstein GmbH, Löwenstein, Germany.
Kurz S; Department of Pneumology, Protestant Lung Hospital, Berlin, Germany.
Griesinger F; Department of Hematology and Oncology, Pius Hospital Oldenburg, Oldenburg, Germany.
Christoph DC; Department of Medical Oncology, West German Cancer Center, University Hospital Essen, Essen, Germany.
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Źródło:
Oncology research and treatment [Oncol Res Treat] 2019; Vol. 42 (5), pp. 243-255. Date of Electronic Publication: 2019 Apr 17.
Typ publikacji:
Journal Article
MeSH Terms:
Compassionate Use Trials*
Immunotherapy*
Carcinoma, Non-Small-Cell Lung/*drug therapy
Lung Neoplasms/*drug therapy
Nivolumab/*therapeutic use
Aged ; Aged, 80 and over ; Antineoplastic Agents, Immunological/adverse effects ; Antineoplastic Agents, Immunological/therapeutic use ; Carcinoma, Non-Small-Cell Lung/therapy ; Clinical Trials as Topic ; Female ; Humans ; Lung Neoplasms/therapy ; Male ; Middle Aged ; Nivolumab/adverse effects ; Progression-Free Survival
Czasopismo naukowe

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