- Tytuł:
-
Efficacy and safety of
compassionate use for rare diseases: a scoping review from 1991 to 2022. - Autorzy:
- Źródło:
- Orphanet journal of rare diseases [Orphanet J Rare Dis] 2023 Nov 28; Vol. 18 (1), pp. 368. Date of Electronic Publication: 2023 Nov 28.
- Typ publikacji:
- Journal Article; Review
- MeSH Terms:
-
Compassionate Use Trials*
Neoplasms*/drug therapy
Humans ; Adult ; Drugs, Investigational/adverse effects ; Rare Diseases/drug therapy ; Drug Approval
Czasopismo naukowe