- Tytuł:
- Oligonucleotide Enhancing Compound Increases Tricyclo-DNA Mediated Exon-Skipping Efficacy in the Mdx Mouse Model.
- Autorzy:
- Źródło:
- Cells [Cells] 2023 Feb 23; Vol. 12 (5). Date of Electronic Publication: 2023 Feb 23.
- Typ publikacji:
- Journal Article; Research Support, Non-U.S. Gov't
- MeSH Terms:
-
Dystrophin */genetics
Oligonucleotides*
Animals ; Mice ; Mice, Inbred mdx ; RNA Precursors ; Oligonucleotides, Antisense/therapeutic use ; DNA ; Exons
Czasopismo naukowe